DOI: 10.1172/jci41615. CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy

CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy

10.1172/jci41615

Crossref journal-article

American Society for Clinical Investigation

Journal of Clinical Investigation (232)

Bibliography

Passini, M. A., Bu, J., Roskelley, E. M., Richards, A. M., Sardi, S. P., OâRiordan, C. R., Klinger, K. W., Shihabuddin, L. S., & Cheng, S. H. (2010). CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy. Journal of Clinical Investigation, 120(4), 1253â1264.

Authors 9

Marco A. Passini (first)
Jie Bu (additional)
Eric M. Roskelley (additional)
Amy M. Richards (additional)
S. Pablo Sardi (additional)
Catherine R. O’Riordan (additional)
Katherine W. Klinger (additional)
Lamya S. Shihabuddin (additional)
Seng H. Cheng (additional)

References 51 Referenced 245

Dates

Type	When
Created	15 years, 5 months ago (March 16, 2010, 2:43 p.m.)
Deposited	2 years ago (Aug. 3, 2023, 1:17 p.m.)
Indexed	3 weeks, 1 day ago (Aug. 7, 2025, 5:03 p.m.)
Issued	15 years, 4 months ago (April 1, 2010)
Published	15 years, 4 months ago (April 1, 2010)
Published Print	15 years, 4 months ago (April 1, 2010)

Funders 0

None

BibTeX

@article{Passini_2010, title={CNS-targeted gene therapy improves survival and motor function in a mouse model of spinal muscular atrophy}, volume={120}, ISSN={0021-9738}, url={http://dx.doi.org/10.1172/jci41615}, DOI={10.1172/jci41615}, number={4}, journal={Journal of Clinical Investigation}, publisher={American Society for Clinical Investigation}, author={Passini, Marco A. and Bu, Jie and Roskelley, Eric M. and Richards, Amy M. and Sardi, S. Pablo and O’Riordan, Catherine R. and Klinger, Katherine W. and Shihabuddin, Lamya S. and Cheng, Seng H.}, year={2010}, month=apr, pages={1253–1264} }

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