DOI: 10.1056/nejmoa0802268. Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

Effect of Gene Therapy on Visual Function in Leber's Congenital Amaurosis

10.1056/nejmoa0802268

Crossref journal-article

Massachusetts Medical Society

New England Journal of Medicine (150)

Bibliography

Bainbridge, J. W. B., Smith, A. J., Barker, S. S., Robbie, S., Henderson, R., Balaggan, K., Viswanathan, A., Holder, G. E., Stockman, A., Tyler, N., Petersen-Jones, S., Bhattacharya, S. S., Thrasher, A. J., Fitzke, F. W., Carter, B. J., Rubin, G. S., Moore, A. T., & Ali, R. R. (2008). Effect of Gene Therapy on Visual Function in Leberâs Congenital Amaurosis. New England Journal of Medicine, 358(21), 2231â2239.

Authors 18

James W.B. Bainbridge (first)
Alexander J. Smith (additional)
Susie S. Barker (additional)
Scott Robbie (additional)
Robert Henderson (additional)
Kamaljit Balaggan (additional)
Ananth Viswanathan (additional)
Graham E. Holder (additional)
Andrew Stockman (additional)
Nick Tyler (additional)
Simon Petersen-Jones (additional)
Shomi S. Bhattacharya (additional)
Adrian J. Thrasher (additional)
Fred W. Fitzke (additional)
Barrie J. Carter (additional)
Gary S. Rubin (additional)
Anthony T. Moore (additional)
Robin R. Ali (additional)

References 24 Referenced 1,516

10.1002/humu.20010
{'key': 'r002', 'first-page': '2735', 'volume': '41', 'author': 'Lorenz B', 'year': '2000', 'journal-title': 'Invest Ophthalmol Vis Sci'} / Invest Ophthalmol Vis Sci by Lorenz B (2000)
10.1007/s00417-004-1020-x
{'key': 'r004', 'first-page': '4293', 'volume': '41', 'author': 'Thompson DA', 'year': '2000', 'journal-title': 'Invest Ophthalmol Vis Sci'} / Invest Ophthalmol Vis Sci by Thompson DA (2000)
10.1038/ng1097-194
10.1038/ng1097-139
10.1073/pnas.95.6.3088
10.1001/archopht.118.4.538 / Arch Ophthalmol by Lotery AJ (2000)
10.1159/000072044
10.1038/3813
10.1074/jbc.M310042200
10.1016/j.cell.2005.06.042
10.1073/pnas.0503460102
10.1073/pnas.0504167102
{'key': 'r015', 'first-page': '1604', 'volume': '43', 'author': 'Znoiko SL', 'year': '2002', 'journal-title': 'Invest Ophthalmol Vis Sci'} / Invest Ophthalmol Vis Sci by Znoiko SL (2002)
10.1167/iovs.03-1302
10.1006/geno.1999.5754
10.1038/88327
10.1167/iovs.02-0595
10.1093/jhered/esg015
10.1038/sj.gt.3302861
10.1371/journal.pmed.0040230
10.1089/hum.1998.9.16-2353
10.2174/1566523054065020

Dates

Type	When
Created	17 years, 4 months ago (April 27, 2008, 8:12 p.m.)
Deposited	8 years, 2 months ago (June 18, 2017, 3:29 a.m.)
Indexed	2 days, 11 hours ago (Aug. 28, 2025, 8:17 a.m.)
Issued	17 years, 3 months ago (May 22, 2008)
Published	17 years, 3 months ago (May 22, 2008)
Published Print	17 years, 3 months ago (May 22, 2008)

Funders 0

None

BibTeX

@article{Bainbridge_2008, title={Effect of Gene Therapy on Visual Function in Leber’s Congenital Amaurosis}, volume={358}, ISSN={1533-4406}, url={http://dx.doi.org/10.1056/nejmoa0802268}, DOI={10.1056/nejmoa0802268}, number={21}, journal={New England Journal of Medicine}, publisher={Massachusetts Medical Society}, author={Bainbridge, James W.B. and Smith, Alexander J. and Barker, Susie S. and Robbie, Scott and Henderson, Robert and Balaggan, Kamaljit and Viswanathan, Ananth and Holder, Graham E. and Stockman, Andrew and Tyler, Nick and Petersen-Jones, Simon and Bhattacharya, Shomi S. and Thrasher, Adrian J. and Fitzke, Fred W. and Carter, Barrie J. and Rubin, Gary S. and Moore, Anthony T. and Ali, Robin R.}, year={2008}, month=may, pages={2231–2239} }

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