DOI: 10.1038/sj.mt.6300200. Spinal Muscular Atrophy: SMN2 Pre-mRNA Splicing Corrected by a U7 snRNA Derivative Carrying a Splicing Enhancer Sequence

Spinal Muscular Atrophy: SMN2 Pre-mRNA Splicing Corrected by a U7 snRNA Derivative Carrying a Splicing Enhancer Sequence

10.1038/sj.mt.6300200

Crossref journal-article

Elsevier BV

Molecular Therapy (78)

Bibliography

Marquis, J., Meyer, K., Angehrn, L., KÃ¤mpfer, S. S., Rothen-Rutishauser, B., & SchÃ¼mperli, D. (2007). Spinal Muscular Atrophy: SMN2 Pre-mRNA Splicing Corrected by a U7 snRNA Derivative Carrying a Splicing Enhancer Sequence. Molecular Therapy, 15(8), 1479â1486.

Authors 6

Julien Marquis (first)
Kathrin Meyer (additional)
Larissa Angehrn (additional)
Sacha S Kämpfer (additional)
Barbara Rothen-Rutishauser (additional)
Daniel Schümperli (additional)

References 49 Referenced 65

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Dates

Type	When
Created	18 years, 3 months ago (May 15, 2007, 10:23 a.m.)
Deposited	5 years, 4 months ago (April 21, 2020, 9:12 p.m.)
Indexed	3 months ago (May 26, 2025, 3:26 a.m.)
Issued	18 years ago (Aug. 1, 2007)
Published	18 years ago (Aug. 1, 2007)
Published Print	18 years ago (Aug. 1, 2007)

Funders 0

None

BibTeX

@article{Marquis_2007, title={Spinal Muscular Atrophy: SMN2 Pre-mRNA Splicing Corrected by a U7 snRNA Derivative Carrying a Splicing Enhancer Sequence}, volume={15}, ISSN={1525-0016}, url={http://dx.doi.org/10.1038/sj.mt.6300200}, DOI={10.1038/sj.mt.6300200}, number={8}, journal={Molecular Therapy}, publisher={Elsevier BV}, author={Marquis, Julien and Meyer, Kathrin and Angehrn, Larissa and Kämpfer, Sacha S and Rothen-Rutishauser, Barbara and Schümperli, Daniel}, year={2007}, month=aug, pages={1479–1486} }

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