DOI: 10.1038/sj.gt.3301955. Viral vector producing antisense RNA restores myotonic dystrophy myoblast functions

Viral vector producing antisense RNA restores myotonic dystrophy myoblast functions

10.1038/sj.gt.3301955

Crossref journal-article

Springer Science and Business Media LLC

Gene Therapy (297)

Bibliography

Furling, D., Doucet, G., Langlois, M.-A., Timchenko, L., Belanger, E., Cossette, L., & Puymirat, J. (2003). Viral vector producing antisense RNA restores myotonic dystrophy myoblast functions. Gene Therapy, 10(9), 795â802.

Authors 7

D Furling (first)
G Doucet (additional)
M-A Langlois (additional)
L Timchenko (additional)
E Belanger (additional)
L Cossette (additional)
J Puymirat (additional)

References 36 Referenced 68

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Mahadevan M et al. Myotonic dystrophy mutation: an unstable CTG repeat in the 3' untranslated region of the gene. Science 1992; 255: 1253–1255. (10.1126/science.1546325) / Science by M Mahadevan (1992)
Fu YH et al. Decreased expression of myotonin–protein kinase mRNA and protein in adult form of myotonic dystrophy. Science 1993; 260: 235–238. (10.1126/science.8469976) / Science by YH Fu (1993)
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Tiscornia G, Mahadevan MS . Myotonic dystrophy: the role of the CUG triplet repeats in splicing of a novel DMPK exon and altered cytoplasmic DMPK mRNA isoform ratios. Mol Cell 2000; 5: 959–967. (10.1016/S1097-2765(00)80261-0) / Mol Cell by G Tiscornia (2000)
Miller JW et al. Recruitment of human muscleblind proteins to (CUG)(n) expansions associated with myotonic dystrophy. EMBO J 2000; 19: 4439–4448. (10.1093/emboj/19.17.4439) / EMBO J by JW Miller (2000)
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Birikh KR, Heaton PA, Eckstein F . The structure, function and application of the hammerhead ribozyme. Eur J Biochem 1997; 245: 1–16. (10.1111/j.1432-1033.1997.t01-3-00001.x) / Eur J Biochem by KR Birikh (1997)
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Scadden AD, Smith CW . Specific cleavage of hyper-edited dsRNAs. EMBO J 2001; 20: 4243–4252. (10.1093/emboj/20.15.4243) / EMBO J by AD Scadden (2001)
Deschenes I et al. Increase in the proliferative capacity of human myoblasts by using the T antigen under the vimentin promoter control. Muscle & Nerve 1997; 20: 437–445. (10.1002/(SICI)1097-4598(199704)20:4<437::AID-MUS6>3.0.CO;2-B) / Muscle & Nerve by I Deschenes (1997)
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Dates

Type	When
Created	22 years, 4 months ago (April 17, 2003, 9:49 a.m.)
Deposited	3 years, 4 months ago (March 29, 2022, 10:06 p.m.)
Indexed	4 months ago (April 22, 2025, 3:12 a.m.)
Issued	22 years, 4 months ago (April 17, 2003)
Published	22 years, 4 months ago (April 17, 2003)
Published Online	22 years, 4 months ago (April 17, 2003)
Published Print	22 years, 3 months ago (May 1, 2003)

Funders 0

None

BibTeX

@article{Furling_2003, title={Viral vector producing antisense RNA restores myotonic dystrophy myoblast functions}, volume={10}, ISSN={1476-5462}, url={http://dx.doi.org/10.1038/sj.gt.3301955}, DOI={10.1038/sj.gt.3301955}, number={9}, journal={Gene Therapy}, publisher={Springer Science and Business Media LLC}, author={Furling, D and Doucet, G and Langlois, M-A and Timchenko, L and Belanger, E and Cossette, L and Puymirat, J}, year={2003}, month=apr, pages={795–802} }

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